Back

4-methylumbelliferone attenuates amyloid pathology and learning deficits in the APP/PS1 mouse model

Amontree, M.; O'Leary, J.; Wonnenberg, P.; Nelson, M.; Conant, K.

2026-05-25 neuroscience
10.64898/2026.05.21.726929 bioRxiv
Show abstract

4-Methylumbelliferone (4-MU) inhibits hyaluronic acid (HA) synthesis and is currently approved in Europe for biliary spasm. 4-MU administration reduces perineuronal nets (PNNs), and enzymatic degradation of PNNs in mouse models of Alzheimers disease (AD) attenuates memory impairment. Although 4-MU has therapeutic efficacy in rodent models of fibrosis and cancer, it has not been examined in an Alzheimers model. Here, we evaluated the impact of long-term 4-MU treatment in the APP/PS1 amyloid mouse model. From three months of age, mice were on either a vehicle or 4-MU-supplemented diet for 70 days or 52 weeks. Short and long-term 4-MU treatment decreased the soluble parenchymal A{beta}1-42/A{beta}1-40 ratio. Reductions in insoluble amyloid plaque were observed following 52 weeks of treatment. Extended 4-MU administration also reduced PNN intensity and ameliorated spatial memory deficits in APP/PS1 mice. These findings provide support for targeting brain extracellular matrix (ECM) as a therapeutic strategy for AD.

Matching journals

The top 8 journals account for 50% of the predicted probability mass.

1
Alzheimer's & Dementia
143 papers in training set
Top 0.5%
17.7%
2
Neurobiology of Disease
134 papers in training set
Top 0.5%
8.5%
3
Alzheimer's Research & Therapy
52 papers in training set
Top 0.2%
7.2%
4
Frontiers in Aging Neuroscience
67 papers in training set
Top 0.8%
4.0%
5
GeroScience
97 papers in training set
Top 0.5%
3.6%
6
Experimental Neurology
57 papers in training set
Top 0.3%
3.3%
7
Alzheimer's & Dementia: Translational Research & Clinical Interventions
16 papers in training set
Top 0.2%
2.9%
8
Scientific Reports
3102 papers in training set
Top 42%
2.9%
50% of probability mass above
9
Acta Neuropathologica Communications
81 papers in training set
Top 0.3%
2.6%
10
Molecular Neurodegeneration
49 papers in training set
Top 0.3%
2.4%
11
Neurobiology of Aging
95 papers in training set
Top 1%
1.7%
12
PLOS ONE
4510 papers in training set
Top 52%
1.7%
13
Journal of Alzheimer's Disease
43 papers in training set
Top 0.8%
1.7%
14
Journal of Alzheimer’s Disease
39 papers in training set
Top 0.7%
1.5%
15
Brain Communications
147 papers in training set
Top 2%
1.3%
16
Brain, Behavior, and Immunity
105 papers in training set
Top 2%
1.3%
17
Molecular Therapy
71 papers in training set
Top 2%
1.3%
18
Molecular Neurobiology
50 papers in training set
Top 0.6%
1.2%
19
Translational Psychiatry
219 papers in training set
Top 3%
1.2%
20
Annals of Neurology
57 papers in training set
Top 2%
1.1%
21
Frontiers in Neuroscience
223 papers in training set
Top 6%
1.0%
22
International Journal of Molecular Sciences
453 papers in training set
Top 11%
1.0%
23
Acta Neuropathologica
51 papers in training set
Top 1.0%
0.9%
24
Advanced Science
249 papers in training set
Top 17%
0.9%
25
The FASEB Journal
175 papers in training set
Top 2%
0.9%
26
Biomedicine & Pharmacotherapy
43 papers in training set
Top 0.9%
0.9%
27
Aging Cell
144 papers in training set
Top 3%
0.8%
28
Journal of Neurochemistry
50 papers in training set
Top 0.6%
0.8%
29
Aging
69 papers in training set
Top 3%
0.8%
30
Alzheimer's & Dementia: Diagnosis, Assessment & Disease Monitoring
38 papers in training set
Top 1%
0.8%