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CYP2D6 variants in amyotrophic lateral sclerosis: an association study of risk and survival
2025-10-06
neurology
Title + abstract only
View on medRxiv
Show abstract
Amyotrophic lateral sclerosis (ALS) is a progressive neurodegenerative disorder with limited therapeutic options. Riluzole remains the only widely available treatment in ALS, yet its benefits are modest and highly variable across patients. Genetic variation in cytochrome P450 2D6 (CYP2D6), a major enzyme in drug metabolism, detoxification of environmental toxins, and biotransformation of endogenous transmitters, has been implicated as a risk factor in neurodegenerative diseases. It has been obse...
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