Back

Polyol pathway dysregulation in CSF links glucose metabolism to tau pathology inde-pendently of amyloid and genetic predisposition

Clos-Garcia, M.; Wretlind, A.; Muk, T.; Hooshmand, K.; Simonsen, A. H.; Winchester, L. M.; Proitsi, P.; Marioni, R. E.; Ahluwalia, T. S.; Kumler, T.; Hasselbalch, S. G.; Legido-Quigley, C.

2026-05-08 neurology
10.64898/2026.05.06.26352559 medRxiv
Show abstract

Dementia affects approximately 60 million people worldwide, yet molecular mechanisms linking early neuropathological changes to clinical progression remain poorly understood. We performed targeted and untargeted metabolomics in plasma and cerebrospinal fluid (CSF) from 166 memory clinic patients spanning no cognitive impairment, mild cognitive impairment due to Alzheimers disease (AD), AD dementia, and mixed AD-cerebrovascular dementia. Using a data-driven approach, we identified a CSF polyol signature characterized by elevated sorbitol, meso-erythritol, and d-glucose/erythritol ratio consistently associated with phosphorylated tau (pTau) and total tau (tTau), but not amyloid-{beta}. This association was validated in an independent CSF metabolomics (n=687) and proteomics (n=737) cohorts. Structural equation modelling confirmed that polyol metabolites predict tau burden, with less than 3% attenuation following genetic adjustment, establishing a non-genetic, metabolically driven mechanism. These findings define a tau-dominant, amyloid-independent metabolic axis in neurodegeneration, implicating the polyol pathway as a potentially modifiable therapeutic target.

Matching journals

The top 3 journals account for 50% of the predicted probability mass.

1
Alzheimer's & Dementia
143 papers in training set
Top 0.4%
21.9%
2
Cell Metabolism
49 papers in training set
Top 0.1%
18.1%
3
Nature Communications
4913 papers in training set
Top 12%
14.0%
50% of probability mass above
4
Brain
154 papers in training set
Top 1%
4.7%
5
Nature Aging
51 papers in training set
Top 0.5%
3.9%
6
Nature Medicine
117 papers in training set
Top 1.0%
3.5%
7
Nature Genetics
240 papers in training set
Top 3%
3.5%
8
Advanced Science
249 papers in training set
Top 8%
2.3%
9
Molecular Neurodegeneration
49 papers in training set
Top 0.4%
2.0%
10
Nature Neuroscience
216 papers in training set
Top 4%
1.6%
11
EMBO Molecular Medicine
85 papers in training set
Top 2%
1.6%
12
eBioMedicine
130 papers in training set
Top 2%
1.4%
13
eLife
5422 papers in training set
Top 48%
1.3%
14
Cell Reports Medicine
140 papers in training set
Top 6%
1.2%
15
Proceedings of the National Academy of Sciences
2130 papers in training set
Top 41%
0.9%
16
Cell Stem Cell
57 papers in training set
Top 2%
0.9%
17
Science Translational Medicine
111 papers in training set
Top 5%
0.9%
18
Nature Biomedical Engineering
42 papers in training set
Top 2%
0.8%
19
Acta Neuropathologica
51 papers in training set
Top 1%
0.8%
20
Nature Metabolism
56 papers in training set
Top 3%
0.7%
21
Molecular Psychiatry
242 papers in training set
Top 4%
0.7%
22
Nature Cancer
35 papers in training set
Top 1%
0.7%
23
Annals of Neurology
57 papers in training set
Top 2%
0.7%
24
Science Advances
1098 papers in training set
Top 34%
0.6%
25
Nature
575 papers in training set
Top 18%
0.6%
26
Med
38 papers in training set
Top 1%
0.6%
27
JCI Insight
241 papers in training set
Top 9%
0.6%