Back

Ligand stabilization enables physiological GITR signaling and antitumor immunity

Admasu, T.; Sadanala, K.; Kalyane, D.; Wang, H.; Yoon, S.; WooHyun, K.; Katiki, M.; Rudnick, J.; Ramachandran, M.; Yu, J.

2026-05-08 cancer biology
10.64898/2026.05.04.722444 bioRxiv
Show abstract

Agonistic antibodies targeting the costimulatory receptor GITR have failed in clinical trials despite a strong preclinical rationale, revealing fundamental limitations of receptor-targeted approaches to TNF superfamily agonism. Here, we demonstrate that pharmacological stabilization of the trimeric structure of human GITRL represents a mechanistically distinct strategy to overcome these limitations. Small-molecule stabilization of GITRL preserves its membrane residency. It enables bidirectional signaling between antigen-presenting cells and T cells, a physiological context that receptor-targeted antibodies bypass through non-physiological clustering of GITR. In humanized GITR/GITRL double-knock-in mice bearing syngeneic tumors, GITRL stabilization expands cytotoxic CD8 T cells, selectively depletes intratumoral regulatory T cells, activates APCs, and restructures the immune spatial architecture. In patient-derived tumor explants, GITRL stabilization reactivates suppressed CD8 T cells in an APC-dependent manner. Our findings establish ligand stabilization as a mechanistically distinct therapeutic strategy and provide a framework for engaging TNF receptor superfamily costimulatory pathways by modulating their native ligands.

Matching journals

The top 7 journals account for 50% of the predicted probability mass.

50% of probability mass above

"Similar papers" are the closest papers from that journal in the model's embedding space. They show what the match is built on, but the ranking comes mostly from a classifier over the whole training set, not from these examples alone.