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Quantifying Somatic Mutation Burden: An Assay Validation Framework and Implementation in SomaticCODEC

Johnstone, J. N.; Phie, J.; Fraser, C.

2026-05-05 genomics
10.64898/2026.04.30.722079 bioRxiv
Show abstract

Validation of somatic mutation burden assays is fundamentally constrained by the absence of a robust ground truth, limiting the interpretability of performance metrics. To address this, we propose a framework based primarily on relative validation, complemented by a suite of secondary metrics aligned to common failure modes. We implement this approach in SomaticCODEC, a ready-to-run assay for quantifying SNV burden in primary human samples, demonstrating strong linearity across mixtures of sperm and blood samples (R2 = 0.91) and high intra-batch precision (CV = 3.3%). This framework provides a practical approach for validating somatic mutation burden assays without requiring a ground truth.

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