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Comparison of methods for assessing effects of risk factors on disease progression in Mendelian randomization under index event bias

2026-03-02 epidemiology Title + abstract only
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Mendelian randomization has emerged as a transformative approach for inferring causal relationships between risk factors and disease outcomes. However, applying Mendelian randomization to disease progression - a critical step in validating pharmacological targets - is hampered by index event bias. This form of selection bias occurs because analyses of disease progression are necessarily restricted to individuals who have already experienced the disease event. Here, we present a comprehensive eva...

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