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Long-Term Slowing of Progression in Huntington's Disease with Pridopidine Treatment
2026-02-17
neurology
Title + abstract only
View on medRxiv
Show abstract
BackgroundHuntingtons disease (HD) causes progressive loss of function, cognition, and motor control, with no approved therapy yet shown to slow disease progression. In the PROOF-HD phase 3 trial, pridopidine did not meet the primary or key secondary outcomes in the overall population, but participants who remained off antidopaminergic medications (ADMs) showed benefits compared to placebo during the double-blind phase. Whether such benefits continue with longer duration treatment and how they c...
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